Alexza and Biovail Form Collaboration to Develop and Commercialize AZ-004 (Staccato(R) Loxapine) in North America
February 10 2010 - 7:00AM
PR Newswire (US)
Conference Call Scheduled for Today -Wednesday, February 10, 2010
at 8:30 a.m. Eastern Time MOUNTAIN VIEW, Calif., Feb. 10
/PRNewswire-FirstCall/ -- Alexza Pharmaceuticals, Inc.
(NASDAQ:ALXA) announced today that it has established a
collaboration with Biovail Laboratories International SRL, a
subsidiary of Biovail Corporation (NYSE:BVF), to develop and
commercialize AZ-004 (Staccato® loxapine) in the U.S. and Canada.
AZ-004 is Alexza's lead program, based on the company's proprietary
technology, the Staccato system. Alexza submitted its New Drug
Application (NDA) for Staccato loxapine in December 2009. Alexza is
seeking regulatory approval to market AZ-004, an inhalation product
candidate developed for the rapid treatment of agitation in
patients with schizophrenia or bipolar disorder. "We are very
excited to be partnering our lead program with Biovail. Their key
strategic focus and their CNS commercial plans match our view of an
ideal partner for AZ-004," said Thomas B. King, Alexza President
and CEO. "We believe that AZ-004, if approved, has the potential to
change the treatment practices for acute agitation, as the only
product able to meet both the patients' desire for quickly and
comfortably gaining control of their agitation, and the clinicians'
goal of rapidly and reliably calming an agitated patient. "This
agreement provides Biovail with a promising late-stage specialty
CNS product," said Bill Wells, Biovail's Chief Executive Officer.
"In clinical studies conducted by Alexza, Staccato loxapine rapidly
delivered drug into the blood stream through the deep lung in a
unique, non-invasive manner. We are delighted to be partnering with
Alexza to bring this important treatment to market." The
collaboration provides for the development and commercialization of
AZ-004 for multiple indications, including the proposed initial
indication of treating agitation in schizophrenia and bipolar
patients, as well as potential future clinical development in
additional psychiatric and neurological indications and the
symptoms associated with these indications. Biovail will lead the
commercialization activities for AZ-004. Alexza will continue to
manage the ongoing AZ-004 NDA review and approval process in
connection with the initial indication, and has entered into a
manufacturing and supply agreement to supply Biovail clinical and
commercial product. Under the terms of the collaboration, Alexza is
entitled to receive an upfront cash payment of $40 million, up to
$90 million in potential milestone payments contingent on the
successful approval of the first AZ-004 NDA, successful commercial
manufacturing scale-up, and the successful completion of additional
clinical trials, regulatory submission (if required) and approval
of an sNDA (if required) in the outpatient setting for patients
with schizophrenia or bipolar disorder. Biovail will make tiered,
royalty payments of 10% to 25% on net commercial sales of AZ-004.
In addition to milestone payments and product royalties, Alexza
will supply AZ-004 to BLS for all of its commercial sales, and will
receive a per-unit transfer price, based upon annual product
volume. About the Agitation Market Opportunity Episodes of
agitation afflict many people suffering from major psychiatric
disorders, including schizophrenia, which affects approximately 2.4
million adults in the United States, and bipolar disorder, which
affects approximately 5.7 million adults in the United States. More
than 90% of these patients will experience agitation in their
lifetime. Agitation generally escalates over time with patients
initially feeling uncomfortable, tense and restless. As the
agitation intensifies, their behavior appears more noticeable to
others as they become threatening and potentially violent,
especially if the agitation is not treated. While patients seek
treatment at different points along this agitation continuum, those
with the most severe symptoms generally require treatment with
injectable drugs in emergency medical settings, and currently are
thought to represent the agitation market. Alexza, however,
believes the therapeutic market for agitation is broader than only
this limited perspective of patients in severe crisis -- many more
are in need of treatment for an agitation episode. Alexza's primary
market research indicates that approximately 50% of treated acute
agitation episodes are treated in emergency settings. Another
approximately 35% of the treated agitation episodes suffered by
schizophrenic and bipolar patients are treated in an inpatient
setting (hospital and long-term residential settings), and
approximately 15% are treated in a physician's office. Alexza's
market research studies with schizophrenia patient caregivers and
bipolar patients indicate these patients currently experience an
average of 11 to 12 episodes of acute agitation each year.
Agitation episodes are currently treated about 55% of the time with
oral antipsychotics and about 45% of the time with intra-muscular,
or IM, injections. Oral medications work relatively slowly, but are
easy to administer, painless and are less threatening to patients.
IM injections have a faster onset of action and a higher
predictability of drug effect, but because they are invasive and
can be frightening to patients, IM injections are usually the
treatment option of last-resort. Currently, no non-invasive
therapies are available that work faster than 30 minutes to help
agitated patients in need of treatment. About AZ-004 (Staccato
loxapine) AZ-004 is an anti-agitation therapeutic that combines
Alexza's proprietary Staccato system with loxapine, a drug
belonging to the class of compounds known generally as
antipsychotics. Loxapine is currently available in an oral
formulation in the U.S. for the management of the manifestations of
schizophrenia. The Staccato system is a hand-held, single-dose
inhaler that delivers a drug aerosol to the deep lung that results
in IV-like pharmacokinetics and rapid systemic effects. As an
easy-to-use, patient-controlled, and highly reliable therapeutic
that provides rapid reduction in agitation, the Company believes
that AZ-004 meets the three key attributes for the treatment of
acute agitation as specified in the American Association of
Emergency Psychiatrists' Expert Consensus Guidelines for the
Treatment of Behavioral Emergencies: speed of onset, reliability of
medication delivery and patient preference. About the Staccato
System Alexza's proprietary Staccato system was rationally designed
to optimally treat acute and intermittent conditions. A single
breath triggers vaporization and delivers a dose of excipient-free
aerosolized, highly bioavailable drug deep into the lungs, where it
is quickly absorbed into the blood stream to begin providing
therapeutic effect. The Staccato system delivers medication that is
comparable to intravenous administration but with greater ease,
patient comfort and convenience. The core of the hand-held Staccato
system is a heat package with a stainless steel substrate, onto
which a thin film of drug is coated. When the patient draws a
single normal breath through the Staccato device, the substrate
surface instantly heats to create an aerosol of optimally-sized,
excipient-free particles of drug that are drawn into the patient's
lungs. The entire Staccato system actuation and drug delivery occur
in less than one second. The Staccato system is unique among
inhalers because it uses no excipients, requires no special
breathing maneuvers and there are no controls to deal with. The
system produces a consistently high emitted dose, regardless of the
patient's breathing pattern, and doses are pre-set. About the size
of a small cell phone, the unit fits easily in a pocket or purse.
Alexza has screened more than 400 drug compounds and more than 200
drug compounds exhibit initial vaporization feasibility with the
Staccato system. Since the filing of its first IND in 2004, Alexza
has dosed more than 2,600 patients and subjects with its Staccato
technology, in 22 different clinical trials under six different
INDs for Staccato-based product candidates. Conference Call
Information Alexza will host a conference call Wednesday morning,
February 10, 2010, at 8:30 a.m. Eastern Time. A replay of the call
will be available for two weeks following the event. The conference
call and replay are open to all interested parties. To access the
conference call via the Internet, go to http://www.alexza.com/,
under the "Investor Relations" link. Please join the call at least
15 minutes prior to the start of the call to ensure time for any
software downloads that may be required. Interested parties may
also pre-register to avoid pre-call delays at
https://www.theconferencingservice.com/prereg/key.process?key=P9GVG9V6A.
To access the live conference call via phone, dial 888.679.8040.
International callers may access the live call by dialing
617-213-4851. The reference number to enter the call is 92719210.
The replay of the conference call may be accessed via the Internet,
at http://www.alexza.com/, or via phone at 888-286-8010 for
domestic callers or 617-801-6888 for international callers. The
reference number for the replay of the call is 93974934. About
Biovail Corporation Biovail Corporation is a specialty
pharmaceutical company engaged in the formulation, clinical
testing, registration, manufacture and commercialization of
pharmaceutical products. Biovail is focused on the development and
commercialization of medicines that address unmet medical needs in
niche specialty central nervous system markets. For more
information about Biovail, visit the Company's web site at
http://www.biovail.com/. About Alexza Pharmaceuticals, Inc. Alexza
Pharmaceuticals is a pharmaceutical company focused on the
research, development and commercialization of novel, proprietary
products for the acute treatment of central nervous system
conditions. Alexza's technology, the Staccato system, vaporizes
unformulated drug to form a condensation aerosol that, when
inhaled, allows for rapid systemic drug delivery through deep lung
inhalation. The drug is quickly absorbed through the lungs into the
bloodstream, providing speed of therapeutic onset that is
comparable to intravenous administration, but with greater ease,
patient comfort and convenience. AZ-004 (Staccato loxapine) is
Alexza's lead program, which is being developed for the rapid
treatment of agitation in schizophrenic or bipolar disorder
patients. Alexza has completed and announced positive results from
both of its AZ-004 Phase 3 clinical trials, and submitted a New
Drug Application submission in December 2009. Alexza has completed
an end-of-Phase 2 meeting with the FDA for AZ-001 (Staccato
prochlorperazine) and has completed two Phase 2 studies with AZ-104
(Staccato loxapine, low-dose). Both product candidates are being
developed for the acute treatment of migraine headache. AZ-002
(Staccato alprazolam) has completed Phase 1 testing and one Phase
2a proof-of-concept clinical trial. Product candidates that have
completed Phase 1 testing are AZ-003 (Staccato fentanyl) for the
treatment of breakthrough pain, and AZ-007 (Staccato zaleplon) for
the treatment of insomnia. More information, including this and
past press releases from Alexza, is available online at
http://www.alexza.com/. Safe Harbor Statement This press release
includes forward-looking statements regarding the development,
therapeutic potential and safety of AZ-004. Any statement
describing a product candidate or Alexza's goals, expectations or
beliefs is a forward-looking statement, as defined in the Private
Securities Litigation Reform Act of 1995, and should be considered
an at-risk statement. Such statements are subject to certain risks
and uncertainties, particularly those inherent in the process of
developing and commercializing drugs. Alexza's forward-looking
statements also involve assumptions that, if they prove incorrect,
would cause its results to differ materially from those expressed
or implied by such forward-looking statements. These and other
risks concerning Alexza's business are described in additional
detail in Alexza's Annual Report on Form 10-K for the year ended
December 31, 2008, and Alexza's other Periodic and Current Reports
filed with the Securities and Exchange Commission, including the
risks under the headings: "We will need substantial additional
capital in the future. If additional capital is not available, we
will have to delay, reduce or cease operations.", "Regulatory
authorities may not approve our product candidates even if they
meet safety and efficacy endpoints in clinical trials." and "If we
enter into strategic partnerships, we may be required to relinquish
important rights to and control over the development of our product
candidates or otherwise be subject to terms unfavorable to us.".
Forward-looking statements contained in this announcement are made
as of this date, and we undertake no obligation to publicly update
any forward-looking statement, whether as a result of new
information, future events or otherwise. DATASOURCE: Alexza
Pharmaceuticals, Inc. CONTACT: Thomas B. King, President & CEO,
+1-650-944-7634, , August J. Moretti, Senior Vice President and
CFO, +1-650-944-7788, , both of Alexza Pharmaceuticals, Inc. Web
Site: http://www.alexza.com/
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